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Table 1 Organ α-gal A activity 26 weeks postinjection (Experiment 1)

From: α-Galactosidase A-Tat Fusion Enhances Storage Reduction in Hearts and Kidneys of Fabry Mice

α-Gal A specific activity (nmol/hr/mg protein)

 

Liver

Spleen

Heart

Kidney

BMa

Brain

Lung

PBS (n = 10)

36 ± 3

135 ± 5

12 ± 1

29 ± 3

53 ± 4

33 ± 1

NDb

LV/enGFP (n = 6)

26 ± 4

111 ± 12

13 ± 2

26 ± 4

58 ± 4 (n = 3)

29 ± 3

117 ± 4 (n = 3)

LV/α-gal A (n = 10)

255 ± 26

328 ± 36

31 ± 2

29 ± 2

66 ± 4 (n = 9)

31 ± 1

113 ± 16 (n = 7)

LV/α-gal A-Tat (n = 10)

310 ± 24

238 ± 34c

35 ± 3

33 ± 3

75 ± 5

30 ± 1

121 ± 18 (n = 7)

WTd (n = 10)

421 ± 22

803 ± 53

89 ± 5

249 ± 10

1481 ± 21

713 ± 26

385 ± 65 (n = 3)

  1. aBM, bone marrow.
  2. bND, not done.
  3. cP < 0.05 vs LV/α-gal A group.
  4. dWT, wild type.